Mucopolysaccharidosis Type I - 128 Studies Found
Completed |
: Safety and Efficacy of Hunterase : Hunter Syndrome : 2012-07-16 : Biological: Hunterase once weekly, 0.5mg/kg IV infusion |
Recruiting |
: Biomarker for Hunter Disease :
|
Recruiting |
: Effects of Adalimumab in Mucopolysaccharidosis Types I, II and VI :
: 2015-05-05 : |
Not yet recruiting |
: Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II :
: 2017-05-11 :
|
Terminated |
: Clinical Trial of Growth Hormone in MPS I, II, and VI :
: Drug: Somatropin (DNA origin) The study starting dose of Nutropin AQ® will be 0.48 mg/kg/week divid |
Active, not recruiting |
: Extension of Study HGT-SAN-055 Evaluating Administration of rhHNS in Patients With Sanfilippo Syndrome Type A (MPS IIIA) : Sanfilippo Syndrome : 2011-02-16 :
|
Completed |
: A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA) : Sanfilippo Syndrome Type A : 2010-01-11 : Other: assessment Physical, developmental, neurological, behavioral, and neurocognitive assessments |
Active, not recruiting |
: Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy :
|
Completed |
: Intracerebral Gene Therapy for Sanfilippo Type A Syndrome :
|